FDA Approves Most Expensive Drug Ever, a $3.5 Million-per-Dose Gene Therapy For Hemophilia B u

Portal Nachrichten

Team IT Sicherheit NEWS (572 Quellen): 30.11.22 Fixes Designänderung und Störung behoben.


➠ FDA Approves Most Expensive Drug Ever, a $3.5 Million-per-Dose Gene Therapy For Hemophilia B

U.S. health regulators this week approved the first gene therapy for hemophilia, a $3.5 million one-time treatment for the blood-clotting disorder. From a report: The Food and Drug Administration cleared Hemgenix, an IV treatment for adults with hemophilia B, the less common form of the genetic disorder which primarily affects men. Currently, patients receive frequent, expensive IVs of a protein that helps blood clot and prevent bleeding. Drugmaker CSL Behring, based in Pennsylvania, announced the $3.5 million price tag shortly after the FDA approval, saying its drug would ultimately reduce health care costs because patients would have fewer bleeding incidents and need fewer clotting treatments. According to a study cited by the National Library of Medicine, the price makes Hemgenix the most expensive medicine in the world, easily topping Novartis' Zolgensma gene therapy for spinal muscular atrophy (SMA), which costs right around $2 million per dose and is also a single-dose medicine. Like most medicines in the U.S., most of the cost of the new treatment will be paid by insurers, not patients, including private plans and government programs. After decades of research, gene therapies have begun reshaping the treatment of cancers and rare inheritable diseases with medicines that can modify or correct mutations embedded in people's genetic code. Hemgenix is the first such treatment for hemophilia and several other drugmakers are working on gene therapies for the more common form of the disorder, hemophilia A.

Read more of this story at Slashdot.

...

➦ IT Security Nachrichten ☆ science.slashdot.org

➠ Komplette Nachricht lesen


Zur Startseite

➤ Ähnliche Beiträge für 'FDA Approves Most Expensive Drug Ever, a $3.5 Million-per-Dose Gene Therapy For Hemophilia B'

FDA Approves Most Expensive Drug Ever, a $3.5 Million-per-Dose Gene Therapy For Hemophilia B

vom 766.14 Punkte
U.S. health regulators this week approved the first gene therapy for hemophilia, a $3.5 million one-time treatment for the blood-clotting disorder. From a report: The Food and Drug Administration cleared Hemgenix, an IV treatment for adults with hemophilia

Psilocybin For Major Depression Granted Breakthrough Therapy By FDA

vom 356.31 Punkte
An anonymous reader quotes a report from New Atlas: The US Food and Drug Administration (FDA) has granted psilocybin therapy a Breakthrough Therapy designation for the second time in a year, this time with a view on accelerating trials testing its efficacy

FDA Approves First Cell-Based Gene Therapy, Becomes Most Expensive Drug In US

vom 353.06 Punkte
An anonymous reader quotes a report from Reuters: The U.S. Food and Drug Administration on Wednesday approved bluebird bio's gene therapy for patients with a rare disorder requiring regular blood transfusions, and the drugmaker priced it at a record $2.8

FDA Approves First-Ever Gene Therapy For Inherited Form of Blindness

vom 333.88 Punkte
schwit1 shares a report from ScienceAlert: In a historic move, the Food and Drug Administration on Tuesday approved a pioneering gene therapy for a rare form of childhood blindness, the first such treatment cleared in the United States for an inherited

FDA Approves ALS Drug Whose Study Was Partly Funded By Ice Bucket Challenge

vom 327.43 Punkte
A new treatment for amyotrophic lateral sclerosis, or ALS, has been approved by the US Food and Drug Administration. CNN reports: The FDA announced approval of Relyvrio, developed by Amylyx Pharmaceuticals, on Thursday. The oral medication works as a

Company Seeks FDA Approval For Single-Dose Drug To Cure HIV/AIDS

vom 326.83 Punkte
"Wednesday night was an exciting one for investors and employees at American Gene Technologies," reports a local Maryland news station. "After years in the making, they submitted a nearly 1,000-page document to FDA. And within its pages just may lie the

FDA Approves First Cell-Based Therapy For Cancer

vom 299.04 Punkte
An anonymous reader quotes a report from NPR: The Food and Drug Administration on Wednesday announced what the agency calls a "historic action" -- the first approval of a cell-based gene therapy in the United States. The FDA approved Kymriah, which scientists

Scientists Dodge FDA To Offer a $1 Million Anti-Aging Treatment in Colombia

vom 266.61 Punkte
Would you pay $1 million and fly to South America for a chance to live longer? From a report: Libella Gene Therapeutics, a Kansas-based company that says it is developing a gene therapy that can reverse aging by up to 20 years, is hoping your answer is

FDA Approves First Drug Derived From Marijuana Plant

vom 264.9 Punkte
The U.S. Food and Drug Administration on Monday approved the first prescription drug derived from the marijuana plant, as a treatment for rare forms of epilepsy that primarily afflict children. From a report: The FDA said Monday that it cleared GW Pharmaceuticals's

FDA Advisers Endorse Gene Therapy To Treat Form of Blindness

vom 229.79 Punkte
An anonymous reader quotes a report from CBS News: A panel of U.S. health advisers has endorsed an experimental approach to treating inherited blindness, setting the stage for the likely approval of an innovative new genetic medicine. A panel of experts

FDA Approves First New Flu Drug In 20 Years

vom 225.97 Punkte
An anonymous reader quotes a report from Popular Science: The Food & Drug Administration just announced that they had approved the aptly-named Xofluza, the first new antiviral drug in two decades, to help alleviate the symptoms of a flu infection.

Price Tag On Gene Therapy For Rare Form of Blindness: $850K

vom 224.68 Punkte
A first-of-its kind genetic treatment for blindness will cost $850,000, less than the $1 million price tag that had been expected, but still among the most expensive medicines in the world. Several readers have shared an Associated Press report: Spark

Team Security Diskussion über FDA Approves Most Expensive Drug Ever, a $3.5 Million-per-Dose Gene Therapy For Hemophilia B